Joanne Kurtzberg, MD – Inborn amino acid metabolism disorder

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<p>The objective of this study is to make T-cell depleted stem cells from a family member who is a half match (haplo-identical) available on an expanded access basis to patients receiving one or two <strong>unrelated cord blood transplants</strong> who are at a higher risk of not engrafting in a safe amount of time. The purpose of the related stem cells is the give the bone marrow a “jump start” towards recovery. Ultimately, the cord blood cells will grow and permanently rescue the bone marrow.</p>